Instagram tag genetherapy

Today I made a quick lunch of cabbage and carrot curry steamed in coconut milk w
Today I made a quick lunch of cabbage and carrot curry steamed in coconut milk with basmati rice. For those of you who missed my Instagram story the other day, my blood level dropped on Palynziq down to a 1.2. I just got these results back a few days ago but they didn't surprise me. On the rare past occasions my levels have gone too low, I always felt very restless and was starting to feel that way this week. That means it's time to increase protein! I was very happy because had been traveling for work the week before my level and was testing my limits as far as intake. My clinic has seen a few level fluctuations even after a very low one, so anything could happen but I'm on the right track. Very thankful that my Palynziq journey has been pretty smooth and uneventful. #lowprotein#noprotein#carbs#basmati#healthy#lunch#eatrealfood#Palynziq#diet#plantbased#curry#cabbage#foodie#raredisease#genetherapy#cleaneating#vegannutrition#foodplanning#mealprep#coconut#phenylketonuria#liveconsciously
24.03.2019 19:16:22
Having only just recovered from a nasty bout of tonsillitis, Michael could easil
Having only just recovered from a nasty bout of tonsillitis, Michael could easily have been forgiven for dipping out of riding the Cheshire Cat Cycling Sportive this morning. While we don’t really use this event as one of our fundraisers, we choose to ride it each year as it’s a local early season event, which we use to kick off yet another year of helping raise awareness of Rett Syndrome and to fundraise for Reverse Rett. With this in mind, Michael wasn’t having any of my suggestion to stay in bed this morning....very much wanting to ride for his little sister. Although it was clear during the ride that he hasn’t fully recovered and he’s now crashed out on the couch. Nonetheless, it was a great, albeit cold and windy ride, for Ciara and Reverse Rett. At the same time we were riding this morning, it was great to see other Team Ciara Cycling riders, Ian Harcourt and Steve Downey repeatedly flogging themselves up and down the Horseshoe Pass as they ramp up the training for their ‘Everesting Cycle Challenge’, scheduled for May 25th. Other big challenges are planned for later this year, which I will post more about in the coming weeks. Thank you to those who continue to support us 👍 #TeamCiara#itsallaboutthegirls#rettsyndrome#ReverseRett#cycling#challenge#training#keepfighting#clinicaltrials#genetherapy#racing2reverserett#ultracycling#ultracyclist#timetrial#sportive#nevergivingup#ridingforhissister
24.03.2019 17:51:40
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Having only just recovered from a nasty bout of tonsillitis, Michael could easil
Having only just recovered from a nasty bout of tonsillitis, Michael could easily have been forgiven for dipping out of riding the Cheshire Cat Cycling Sportive this morning. While we don’t really use this event as one of our fundraisers, we choose to ride it each year as it’s a local early season event, which we use to kick off yet another year of helping raise awareness of Rett Syndrome and to fundraise for Reverse Rett. With this in mind, Michael wasn’t having any of my suggestion to stay in bed this morning....very much wanting to ride for his little sister. Although it was clear during the ride that he hasn’t fully recovered and he’s now crashed out on the couch. Nonetheless, it was a great, albeit cold and windy ride, for Ciara and Reverse Rett. At the same time we were riding this morning, it was great to see other Team Ciara Cycling riders, Ian Harcourt and Steve Downey repeatedly flogging themselves up and down the Horseshoe Pass as they ramp up the training for their ‘Everesting Cycle Challenge’, scheduled for May 25th. Other big challenges are planned for later this year, which I will post more about in the coming weeks. Thank you to those who continue to support us 👍 #TeamCiara#itsallaboutthegirls#rettsyndrome#ReverseRett#cycling#challenge#training#keepfighting#clinicaltrials#genetherapy#racing2reverserett#ultracycling#ultracyclist#timetrial#sportive#nevergivingup#ridingforhissister
24.03.2019 17:45:19
Compartimos el documental realizado por la Fundación Isabel Gemio que narra la h
Compartimos el documental realizado por la Fundación Isabel Gemio que narra la historia de todos aquellos que, cada día, se enfrentan a enfermedades poco comunes y que aún son ‘invisibles’ para el resto de la sociedad. Este documental busca hacer visible lo invisible, y dar voz a los que luchan por dar visibilidad, concienciar frente a sus enfermedades y promover la investigación para encontrar un tratamiento. . . . #musculardistrophy#asociacióndistrofiamusculardecinturas#rarediseases#sarcoglicanopathy#degenerativediscdisease#LGMD#CureLGMD#greenlimelgmd#LGMDassociation#respect#genetherapy#investigation#TogetherWeAreStrongers
23.03.2019 20:55:21
The more research done on determining the cause of rare diseases will lead to ad
The more research done on determining the cause of rare diseases will lead to advances in our understanding of other common diseases such as cancer, heart disease, diabetes, stroke, and other major health problems that affect millions worldwide. However, rare diseases represent a large medical challenge due to the lack of financial incentives to treat or cure rare diseases . . . #BluGenesFdn#babies#children#raredisease#taysachsdisease#infant#blugenes#geneticdisorder#infancy#hope#taysachs#showyourrare#rarediseaseawareness#care4rare#awareaboutrare#rarewarrior#genetherapy#research#UMASS#donation#cure#umassmed#linkinprofile#therapy
23.03.2019 20:00:10
Sing us a song, you’re the piano man 🎶 @lucias_sarto took me back to the 20s wit
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Sing us a song, you’re the piano man 🎶 @lucias_sarto took me back to the 20s with this star 🌟 head band, feather & fur! • • • • • • #fundraiser#gala#downtown#kc#thepresident#powerandlight#piano#pianoman#eltonjohn#music#genetherapy#roaring20s#20s#flapper#fashion#era#ootn
23.03.2019 16:04:01
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📣 📣📣📣📣📣📣📣 AIU has exciting news, Adrenas Therapeutics, a BridgeBio company, will
📣 📣📣📣📣📣📣📣 AIU has exciting news, Adrenas Therapeutics, a BridgeBio company, will be participating in our conference this year. Adrenas is in the pre-clinical stages of developing a potential gene therapy for CAH. Some of Adrenas’ team will be attending our conference and are keen to meet with CAH community members to learn more about living with CAH, to share more about the science and the potential for therapy(ies) of this type, and to answer whatever questions they can. AIU is thrilled and thankful to be included and eagerly anticipate learning more about the process! . . . Conference link in the bio! Deadline to register is March 25th!!!! . . #cah#congenitaladrenalhyperplasia#adrenalinsufficiency#adrenalinsufficiencyawareness#genetherapy#hopeforacure#futureofmedicine#aiu
23.03.2019 15:55:59
We are less than a week from this epic gathering.  We are excited.  We are hopef
We are less than a week from this epic gathering. We are excited. We are hopeful. Let’s do this! #endnf2#genetherapy#medicalresearch#neurofibromatosistype2#ineedacure#nevergiveup
23.03.2019 15:49:27
Let's do this!
Excited to be part of this momentous meeting to #EndNF2 with @nf2
Let's do this! Excited to be part of this momentous meeting to #EndNF2 with @nf2biosolutions#ineedacure#neurofibromatosistype2#genetherapy
23.03.2019 15:23:51
In honor of #PurpleDay, an anonymous donor will match the first $2,000 donated f
In honor of #PurpleDay, an anonymous donor will match the first $2,000 donated from now through the end of March! Purple Day is an international epilepsy awareness day. Wear purple on March 26! 💜💜💜 #uld#unverrichtlundborgdisease#raredisease#epilepsyawareness#uldawareness#genetherapy#hopeforuld
23.03.2019 14:59:16
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In honor of #PurpleDay, an anonymous donor will match the first $2,000 donated f
In honor of #PurpleDay, an anonymous donor will match the first $2,000 donated from now through the end of March! Purple Day is an international epilepsy awareness day. Wear purple on March 26! 💜💜💜 #uld#unverrichtlundborgdisease#raredisease#epilepsyawareness#uldawareness#genetherapy#hopeforuld
23.03.2019 14:59:16
Mice are able to see how they run thanks to gene therapists at UC Berkeley, and
Mice are able to see how they run thanks to gene therapists at UC Berkeley, and it looks promising for macular degeneration patients as well. ⠀ ⠀ Read more: https://buff.ly/2OkDK2E ⠀ #GeneTherapy#AMD#ganglioncells
23.03.2019 14:10:31
Gene therapy aims to cure illness that mistaken gene. Here to see how the immune
Gene therapy aims to cure illness that mistaken gene. Here to see how the immune system treatment works in children. 🧬💉🔬 #immunesystem#choromosomalabnormality#genetherapy#exvivo#invivo#bonemorrowcells#biology#molecularbiology#lifescience#genetics#happydays#instalike#instagood Reference: www.xlpresearchtrust.org.tr
23.03.2019 09:22:47
She’s loaded with eggs, 🤞🤞, Black Pastel Mojave Trick x Hypo, he’s due to lay ne
She’s loaded with eggs, 🤞🤞, Black Pastel Mojave Trick x Hypo, he’s due to lay next Friday! This clutch holds some tremendous pieces for future projects. #snakensteinreptiles#genetherapy#ballpythonsofinstagram#ballpythonmorphs#python#ballpythonbreeder#snakesofinstagram#snake#ballpython
23.03.2019 07:01:49
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Another fresh shed on this gorgeous boy! Fire Leopard Het Clown, he’s almost 500
23.03.2019 06:59:54
Love love love love this girl! She just glows after every shed, shed 2 days ago.
Love love love love this girl! She just glows after every shed, shed 2 days ago. Look at that belly pattern, and the red flecks in there 😍. Fire Spark Clown #snakensteinreptiles#genetherapy#ballpythonsofinstagram#ballpythonmorphs#python#ballpythonbreeder#snakesofinstagram#snake#ballpython#arsonistballpython
23.03.2019 06:56:55
Squeezed one more pairing in for these two. Mystic Vanilla x Enchi Vanilla Spide
Squeezed one more pairing in for these two. Mystic Vanilla x Enchi Vanilla Spider, we’re extremely excited for this pairing! #snakensteinreptiles#genetherapy#ballpythonsofinstagram#ballpythonmorphs#python#ballpythonbreeder#snakesofinstagram#snake#ballpython
23.03.2019 04:05:39
INTERPHEX 2019 delivers Innovation and Technology!

Focus on exhibits and demons
INTERPHEX 2019 delivers Innovation and Technology! Focus on exhibits and demonstrations on cell processing, gene therapy and Pharma 4.0 technologies. Don’t miss Technical Conference compliments of Pall Biotech and Happy Hour with @GermfreeLabs. Check out the new tech launches! Contact your favorite supplier to register or click here and save the onsite fee! www.interphex.com/Register/ #INTERPHEX#SmartManufacturing#cellprocessing#genetherapy#Pharmaceutical#Bioprocessing#Pharma4.0#INNOPHEX@Tweet_IPS#40Years#Bio#pharmaceuticalprocessing#pharmaceuticalpackaging#PharmaceuticalInnovation#SartoriusGlobal#ProteinForm#BioSpherix#GermFreeLabs#GermfreeLaboratories#Manufacturing#celltherapy
22.03.2019 19:00:20
We’re committed to the highest level of transparency! Our organization earned a
We’re committed to the highest level of transparency! Our organization earned a 2019 Platinum Seal of Transparency, showcasing the progress and results we’re making toward our mission! 👏 👏 👏
22.03.2019 17:06:16
#FeatureFriday - Meet Dr. Job Dekker (PhD), Professor of Biochemistry and Molecu
#FeatureFriday - Meet Dr. Job Dekker (PhD), Professor of Biochemistry and Molecular Pharmacology at #UMassMed. In 2012, Dr. Dekker led a team to help conclusively prove that the 3rd structure of chromosomes plays a significant role in cancer genomics. . Click the link in our bio to read more on how #BluGenesFdn is supporting gene therapy research at #UMassMedical [https://bit.ly/2SPq41m] . . . #BluGenesFdn#babies#children#raredisease#taysachsdisease#infant#blugenes#geneticdisorder#infancy#hope#taysachs#showyourrare#rarediseaseawareness#care4rare#awareaboutrare#rarewarrior#genetherapy#research#UMASS#donation#cure#umassmed#linkinprofile#therapy#featurefriday#stafffeature
22.03.2019 17:00:19
Learn about how #mousemodels were used to gain "night vision," identify which st
22.03.2019 13:46:00
A UT Southwestern gene therapy program is playing a leading role in this effort,
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A UT Southwestern gene therapy program is playing a leading role in this effort, trailblazing a series of clinical trials for diseases in which a single gene missing from the patient’s DNA can be packaged into a virus and delivered into brain cells.⠀ ⠀ The scientists have harnessed adenoassociated virus (AAV) as their best hope. Once the harmless virus is loaded with the missing gene, it is injected into fluid in the spine, allowing it to reach the brain.⠀ ⠀ To speed development and refinement of this therapy, the program has established one of the nation’s few facilities to manufacture AAV for patient use.⠀ ⠀ “Our work here is changing medicine,” said Dr. Steven Gray, who is coordinating with the Food and Drug Administration to arrange a clinical trial to test a treatment for Willow’s disease, hopefully by late this year. “Now we’re in a rather unique position to help families who may not have had much hope."⠀ ⠀ Source: UT Southwestern Annual Report⠀ ⠀ #CureMSD#TogetherWeCan#RareDisease#GeneTherapy#RareNotAlone#UTSouthwestern#CareAboutRare#DNA
22.03.2019 13:00:43
UCSF researchers report promising findings from the first gene therapy trial for
UCSF researchers report promising findings from the first gene therapy trial for Parkinson’s disease in which intra-operative MRI-guided monitoring was used to guide infusion of treatment into the brain. This technique was developed by Krys Bankiewicz, MD, PhD in the Dept of Neurosurgery. In this Phase I clinical trial, 15 patients saw up to three hours of extra 'on-time' daily, referring to when their medication was effective without causing dyskinesia. The patients were also able to reduce their medication by up to 42%, and experienced increased mobility. Parkinson's disease occurs when specific dopamine-producing cells in the substantia nigra (a part of the brain involved in movement) start to die. The drug levodopa is initially effective in addressing symptoms, since it gets converted into dopamine and compensates for the lost cells. However, levodopa loses effectiveness over the course of the disease, when AADC, the enzyme that converts levodopa to dopamine, starts to decline as well. Bankiewicz and colleagues have pioneered the use of gene therapy to address the decreased availability of this critical enzyme. Using an inactive, modified virus, the AADC gene is delivered directly to the basal ganglia by guiding a catheter through small holes in the skull. Phase II of the study, which will allow us to better understand the safety and effectiveness of the gene therapy, is currently underway. Read more at the link in our profile ⬆️. . 📷: Two of the co-authors, UCSF neurosurgeon Paul Larson, MD (left) and Alistair Martin, PhD, (right) with the ClearPoint SmartFrame device they developed which allows for the placement and operation of instruments during neurosurgical procedures utilizing intra-operative MRI. Not pictured, other co-authors including Krys Bankiewicz MD, PhD and Chad Christine, MD. #neurosurgery#neurosurgeon#research#physicianscientist#scientist#neuroscientist#clinicaltrials#genetherapy#parkinsons#parkinsonsdisease#parkinsonsawareness#ucsfneurosurgery#ucsfneurosurgeon#ucsfresearch#ucsf
21.03.2019 20:28:01
#BluGenesFdn is supporting #UMassMedical to bring #TaySachs gene therapy approac
#BluGenesFdn is supporting #UMassMedical to bring #TaySachs gene therapy approach to clinical trial! #UMassMed is home to one of the leading gene therapy centres in the world and the greatest collection of RNA-focused scientists. Read more on how we are working together. Link in bio [https://bit.ly/2Qd9gmq] . . . #BluGenesFdn#babies#children#raredisease#taysachsdisease#infant#blugenes#geneticdisorder#infancy#hope#taysachs#showyourrare#rarediseaseawareness#care4rare#awareaboutrare#rarewarrior#genetherapy#research#UMASS#donation#cure#umassmed#linkinprofile#therapy
21.03.2019 19:00:18
Maybe 2nd best 😂
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Maybe 2nd best 😂...more
21.03.2019 18:30:47
Debuting at INTERPHEX, INNOPHEX, in collaboration with IPS, offers cell processi
Debuting at INTERPHEX, INNOPHEX, in collaboration with IPS, offers cell processing, gene therapy and Pharma 4.0 solutions, exhibits, demonstrations, Technical Conference with Foundation Sponsor Pall Biotech and a Networking Happy Hour with Germfree. An exciting, can’t miss event! Register today. https://www.interphex.com/Register/ #INTERPHEX#SmartManufacturing#cellprocessing#genetherapy#Pharmaceutical#Bioprocessing#Pharma4.0#INNOPHEX@Tweet_IPS#40Years#Bio#pharmaceuticalprocessing#pharmaceuticalpackaging#PharmaceuticalInnovation
21.03.2019 18:00:16
21.03.2019 17:57:44
Twist and roll, roll them eggs that way! A sign of good things to come! HRA x Pa
21.03.2019 17:18:12
We are excited to be sponsoring the Alliance for Regenerative Medicine Cell & Ge
We are excited to be sponsoring the Alliance for Regenerative Medicine Cell & Gene Therapy Investor Day in NYC today. See you there! #genetherapy#celltherapy#regenerativemedicine#science#crossoversearch#gene#genomeediting#nyc#medicine#health#lifesciences#event#armevents#investor#investorday
21.03.2019 16:59:10
CRB Tech Tank program @INTERPHEX! CRB experts share insight: “Isolators for Cell
CRB Tech Tank program @INTERPHEX! CRB experts share insight: “Isolators for Cell/Gene Therapy”, “State-of-the-Art Phase 3 Commercial Gene Therapy Facilities” and “The Future of Cell/Gene Therapy”. All you need to do is Register to attend the 40th Anniversary of INTERPHEX. Just 2 weeks! Did YOU register yet? www.interphex.com/Register/ @INTERPHEX#SmartManufacturing#cellprocessing#genetherapy#pharma#bio#celltherapy#Pharmaceutical#Bioprocessing#Pharma4.0@INNOPHEX#cellandgenetherapy@CRB_USA#40Years#Bio#pharmaceuticalpackaging#Top20Under40#YoungProfessionals#designtrends#PharmaceuticalInnovation
21.03.2019 15:00:21
People left blind by retinal degeneration have one option: electronic eye implan
People left blind by retinal degeneration have one option: electronic eye implants. Neuroscientists have now developed an alternative: gene therapy that, in tests, restored vision in blind mice. A gene for green opsin delivered via virus gave blind mice enough sight to discern patterns on an iPad at a resolution sufficient for humans to read. University of California - Berkeley. Science Daily 2019 @ucberkeleyofficial Learn more about all things #Medicine and #RegenerativeMedicine. Follow us @regenmed101.#DoctorYu#RegenMed101#RegenerativeMedicine#Regeneration#Doctors#Physicians#classisinsession#genetherapy#healthcare#healthtalk#digitalhealth#FOAmed#MEDed#mhealth#instahealth#menshealth#womenshealth#equalhealth#crispr#gene#genetherapy#virus
21.03.2019 13:25:13
Approximately 1 in 9 women in the United States experiences symptoms of postpart
Approximately 1 in 9 women in the United States experiences symptoms of postpartum depression, according to the Centers for Disease Control and Prevention Now, the U. S. Food and Drug Administration (FDA) has approved brexanolone, an analog of the endogenous human hormone allopregnanolone and the first drug specifically designed to treat postpartum depression. NIH news release 2019. Learn more about all things #Medicine and #RegenerativeMedicine. Follow us @regenmed101.#DoctorYu#RegenMed101#hbot#hyperbaric#RegenerativeMedicine#Regeneration#Doctors#Physicians#classisinsession#genetherapy#healthcare#healthtalk#digitalhealth#FOAmed#MEDed#mhealth#instahealth#menshealth#womenshealth#equalhealth#brexanolone#postpartumdepression
21.03.2019 13:19:13
She’s on the defensive, expecting mom to be, first time girl, t minus 4 days for
She’s on the defensive, expecting mom to be, first time girl, t minus 4 days for eggs, if she’s on schedule 😂. Mystic Vanilla x Mojave #snakensteinreptiles#genetherapy#ballpythonsofinstagram#ballpythonmorphs#python#ballpythonbreeder#snakesofinstagram#ballpython#snake
21.03.2019 07:12:44
'People left blind by retinal degeneration have one option: electronic eye impla
'People left blind by retinal degeneration have one option: electronic eye implants. Neuroscientists have now developed an alternative: gene therapy that, in tests, restored vision in blind mice. A gene for green opsin delivered via virus gave blind mice enough sight to discern patterns on an iPad at a resolution sufficient for humans to read. Given existing AAV eye therapies already approved, this new therapy could be ready for clinical trials in three years.' - Sciencedaily 🌐 For more info: https://www.sciencedaily.com/releases/2019/03/190315095808.htm #neuroscience#genetherapy#nextgenescientific
21.03.2019 06:03:59
😂
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21.03.2019 04:43:36
This girl gets stronger everyday! It is such a joy to see her gaining more mobil
This girl gets stronger everyday! It is such a joy to see her gaining more mobility. #bellasbumbas#babywheelchair#newmuscles#lookathergo#spinraza#genetherapy#newgene#smatype1#mobility
21.03.2019 01:54:06
Japan (@japan ) has issued draft guidelines that allow the use of gene-editing t
Japan (@japan ) has issued draft guidelines that allow the use of gene-editing tools in human embryos. The proposal was released by an expert panel representing the country’s health and science ministries on Sept 2018. Although the country regulates the use of human embryos for research, there have been no specific guidelines on using tools such as CRISPR–Cas9 to make precise modifications in their DNA until now. Manipulating DNA in embryos could reveal insights into early human development. Researchers also hope that in the long term, these tools could be used to fix genetic mutations that cause diseases, before they are passed on. But the editing of genes in human embryos, even for research, has been controversial. Ethicists and many researchers worry that the technique could be used to alter DNA in embryos for non-medical reasons. Many countries ban the practice, allowing gene-editing tools to be used only in non-reproductive adult cells. Nature 2018 Learn more about all things #Medicine and #RegenerativeMedicine. Follow us @regenmed101.#DoctorYu#RegenMed101#hbot#hyperbaric#RegenerativeMedicine#Regeneration#Doctors#Physicians#classisinsession#genetherapy#healthcare#healthtalk#digitalhealth#FOAmed#MEDed#mhealth#instahealth#menshealth#womenshealth#equalhealth#crispr#gene
21.03.2019 00:10:20
Heading off to her new home! Short adventure, down the road to Dallas,Tx. Safe t
Heading off to her new home! Short adventure, down the road to Dallas,Tx. Safe travels little one, we know your new owner is excited! #snakensteinreptiles#genetherapy#ballpythonsofinstagram#ballpythonmorphs#python#ballpythonbreeder#snakesofinstagram#ballpython#snake
20.03.2019 23:31:59
📢 Calling EVERYONE & ANYONE with big ♥!⁣ ⁣
⠀ ⠀ ⠀ ⠀ ⠀ ⠀ ⠀ ⠀ ⠀ ⠀ ⠀ ⠀
💪 Let’s #smas
📢 Calling EVERYONE & ANYONE with big ♥!⁣ ⁣ ⠀ ⠀ ⠀ ⠀ ⠀ ⠀ ⠀ ⠀ ⠀ ⠀ ⠀ ⠀ 💪 Let’s #smashSMARD & SAVE LIVES together! DONATE TODAY via the link in our bio! ⁣ ⠀ ⠀ ⠀ ⠀ ⠀ ⠀ ⠀ ⠀ ⠀ ⠀ ⠀ ⠀ 🔬Gene Therapy IS the solution, but it’s VERY expensive. $3 million expensive! EVERY PENNY COUNTS & Will fund SMARD1 #GeneTherapy research at Nationwide Children’s Hopsital ⁣ ⁣ ⠀ ⠀ ⠀ ⠀ ⠀ ⠀ ⠀ ⠀ ⠀ ⠀ ⠀ ⠀ 📚 To learn more, please like Smash SMARD or visit www.smashSMARD.org ⁣ ⁣ ⠀ ⠀ ⠀ ⠀ ⠀ ⠀ ⠀ ⠀ ⠀ ⠀ ⠀ ⠀ ⭐ Please participate, donate, and NOMINATE AS MANY PEOPLE AS POSSIBLE!! Copy and paste the body in the comments of your post! ⭐
20.03.2019 23:25:05
💡DID YOU KNOW? Between 1973-83, fewer than 10 treatments for #rarediseases were
💡DID YOU KNOW? Between 1973-83, fewer than 10 treatments for #rarediseases were approved. Since 1983, the Office of Orphan Products Development (OOPD) program helped develop and bring 400+ drugs and biologic products for rare diseases to market . . . #BluGenesFdn#babies#children#raredisease#taysachsdisease#infant#blugenes#geneticdisorder#infancy#hope#taysachs#showyourrare#rarediseaseawareness#care4rare#awareaboutrare#rarewarrior#genetherapy#research#UMASS#donation#cure#umassmed#linkinprofile#therapy
20.03.2019 21:00:32
Charcot Marie Tooth disease – also known as CMT – has nothing to do with teeth.
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Charcot Marie Tooth disease – also known as CMT – has nothing to do with teeth. The disease – which shares many of the same symptoms as amyotrophic lateral sclerosis (#ALS) – causes progressive muscle weakness and loss of motor skills. Eventually the diaphragm becomes too weak to breathe. UT Southwestern is collaborating with a Massachusetts family to organize a #genetherapy clinical trial to treat the condition. The clinical trial is among several that #UTSouthwestern’s gene therapy program is organizing for a class of rare #neurological diseases largely overlooked by the medical field. #RareDisease#utswdiscovery#utswneurology#pioneering#groundbreaking#utswbrain
20.03.2019 20:15:16
New blog post just published 
#genetherapy #blog #new_post #technology #Wed_post
20.03.2019 19:46:10
Simple, so clean, love her blushings, a Ghost we hatched last year. Can never ha
Simple, so clean, love her blushings, a Ghost we hatched last year. Can never have too many females, especially recessive. 😉#snakensteinreptiles#genetherapy#ballpythonsofinstagram#ballpythonmorphs#python#ballpythonbreeder#snakesofinstagram#snake#ballpython
20.03.2019 19:05:57
This year’s #AACR19 conference will highlight some of the best in #cancerresearc
This year’s #AACR19 conference will highlight some of the best in #cancerresearch 🔬. We’ll be sharing results from our #pancreaticcancer trial that combines #immunotherapy with standard-of-care chemo, 📊our CEO Jeff Bluestone will be honored with the prestigious AACR-Irving Weinstein Lectureship, 🏆and there will be exciting research around the #microbiome-#cancer connection along with #celltherapy and #genetherapy discoveries. 🧬See our highlights on the agenda 👩🏻‍🔬at www.parkerici.org
20.03.2019 14:33:53
Hace años cuando Vivet solo era un business plan en Columbus no nos podíamos ima
Hace años cuando Vivet solo era un business plan en Columbus no nos podíamos imaginar que se llegaría tan lejos. Grandes noticias para los pacientes de Wilson y enorme el equipo. Enhorabuena!! . Pfizer Adds to Big Pharma’s Gene-Therapy Deal Streak . #genetherapy
20.03.2019 14:12:36
Type 1 diabetes occurs when the pancreas produces little or none of the insulin
Type 1 diabetes occurs when the pancreas produces little or none of the insulin needed to regulate blood glucose. Type 2 diabetes occurs when the pancreas does not produce enough insulin or the body becomes resistant to the insulin that is present. Patients with type 1 diabetes and some patients with type 2 diabetes inject insulin, and occasionally glucagon, to regulate their blood glucose, which is critical to lower their risk of long-term complications such as blindness, kidney failure and cardiovascular disease. When managing diabetes, many patients must vigilantly test blood glucose with a glucose meter, calculate insulin doses, and administer necessary insulin doses with a needle or insulin infusion pump to lower blood glucose. Glucagon may be injected in an emergency to treat severe low blood glucose. Some patients benefit from additional monitoring with a continuous glucose monitoring system The Artificial Pancreas Device System is a system of devices that closely mimics the glucose regulating function of a healthy pancreas. Most Artificial Pancreas Device Systems consists of three types of devices already familiar to many people with diabetes: a continuous glucose monitoring system (CGM) and an insulin infusion pump. A blood glucose device (such as a glucose meter) is used to calibrate the CGM. Learn more about all things #Medicine and #RegenerativeMedicine. Follow us @regenmed101.#DoctorYu#RegenMed101#hbot#hyperbaric#RegenerativeMedicine#Regeneration#Doctors#Physicians#classisinsession#genetherapy#healthcare#healthtalk#digitalhealth#FOAmed#MEDed#mhealth#instahealth#menshealth#womenshealth#equalhealth#diabetes
20.03.2019 13:28:21
Scientist at UC Berkeley used Adeno-associated viruses (AAV) to insert a gene fo
Scientist at UC Berkeley used Adeno-associated viruses (AAV) to insert a gene for green-light receptors in the eyes of blind mice and a month later they were able to see motion, brightness and were able to discern patterns on an iPad. This could be a potential new therapy for people left blind by retinal degeneration. Credit: John Flannery, UC Berkeley DOI: 10.1038/s41467-019-09124-x . #science#scienceandtechnology#sciencecommunication#scicomm#research#tech#technology#genetics#genetherapy#viruses#virusresearch#ucberkeley
20.03.2019 12:41:33
After a busy first day at the Bioprocessing Summit in Lisbon - We are on again!
After a busy first day at the Bioprocessing Summit in Lisbon - We are on again! Our Senior Scientist and Ph. D. Vanessa Carvalho will hold a presentation later on today, at 15:15 on the topic - Analysis of Purity and Packaging of Gene Therapy Vectors and VLPs to Support Process Development Decisions. Make sure to attend! Make sure to team up with us at our booth today and tomorrow and share your impressions, insights and challenges! Least but not last, check out our MiniTEM™ - A compact and portable TEM. Designed for automated nanoparticle characterization. Built by experts for every day users. Bringing software, AI, Big Data and Life Science data into the equation. Makining the invisible visible. Hope to see you there! Team Vironova Nina Forsberg Beata Hadavand Bas Hersmus Lennart Lindqvist __________ #BPSMTeu#lisbon#biotech#vironova#lifesciences#bioprocessing#makingtheinvisiblevisible#transmissionelectronmicroscopy#genetherapy#MiniTEM#electronmicroscope#transmissionelectonmicroscopemicroscopist#research#biosafety#microbiology#science#medtech#lifescience
20.03.2019 09:15:49
Thank you all for following me @RegenMed101. 
Many of you have asked who I am. I
Thank you all for following me @RegenMed101. Many of you have asked who I am. I wanted to post this to share my educational background with you. I graduated college in 3 years with 2 Degrees @northcarolina, I then spent the next 4 years in a research laboratory doing advanced and next level technology working with multiple Nobel Prize Laureate @nihgov. I furthered my education by going to medical school in Pennsylvania and then completing internship and residency, where I have trained at over 15 hospital sites ranging from @weillcornell, @nyulangone, @hspecialsurgery, @sloankettering and more. I started this educational forum to showcase one of my many interests in #regenerativemedicine. I present facts and dispel the myths. Learn more about all things Medicine, using language that anybody can understand. Feel free to ask questions and comment on our posts. (Just give me a few days to respond, as I’m always working in making medicine better for my patients) Learn more about all things #Medicine and #RegenerativeMedicine. Follow us @regenmed101.#DoctorYu#RegenMed101#hbot#hyperbaric#RegenerativeMedicine#Regeneration#Doctors#Physicians#classisinsession#genetherapy#healthcare#healthtalk#digitalhealth#FOAmed#MEDed#mhealth#instahealth#menshealth#womenshealth#equalhealth
20.03.2019 03:21:44
Congrats to @pierluigiparacchi for winning the SQUINTO-LEPERA AWARD: Pierluigi c
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Congrats to @pierluigiparacchi for winning the SQUINTO-LEPERA AWARD: Pierluigi co-founded Genenta Science,a clinical stage immune-gene therapy company which leverages the ground-breaking science from Professor Naldini at the San Raffaele Milano hospital. ——— Genenta has phase 1 / 2 trials ongoing in multiple myeloma and glioblastoma. —- We know that Pierluigi Peracchi will make great strides in the field of oncology. #LBHAward19#immunotherapy#genetherapy#phenotypes#genotypes#genetherapy#turnyourlyfeon#familyforlyfe#lyfebulbhelsinn2019
19.03.2019 22:15:38
CRISPR technology is a simple yet powerful tool for editing genomes. It allows r
CRISPR technology is a simple yet powerful tool for editing genomes. It allows researchers to easily alter DNA sequences and modify gene function. Its many potential applications include correcting genetic defects, treating and preventing the spread of diseases and improving crops. However, its promise also raises ethical concerns. "CRISPR" stands for "clusters of regularly interspaced short palindromic repeats." It is a specialized region of DNA with two distinct characteristics: the presence of nucleotide repeats and spacers. Repeated sequences of nucleotides — the building blocks of DNA — are distributed throughout a CRISPR region. Spacers are bits of DNA that are interspersed among these repeated sequences. CRISPR technology has also been applied in the food and agricultural industries to engineer probiotic cultures and to vaccinate industrial cultures (for yogurt, for example) against viruses. It is also being used in crops to improve yield, drought tolerance and nutritional properties. Stay up to date on what makes Regenerative Medicine a new and legitimate field and not just a trend. Learn more by following us @regenmed101.#DoctorYu#RegenMed101#hbot#hyperbaric#RegenerativeMedicine#Regeneration#Doctors#Physicians#classisinsession#genetherapy#crispr#gene#dna#rna#healthcare#healthtalk#digitalhealth#FOAmed#MEDed#mhealth#instahealth
19.03.2019 21:41:48
Crossover Search is sponsoring the Alliance for Regenerative Medicine Investor D
Crossover Search is sponsoring the Alliance for Regenerative Medicine Investor Day in NYC this Thursday, March 21st. For more info, check out arminvestorday.com #genetherapy#celltherapy#regenerativemedicine#science#crossoversearch#gene#genomeediting#nyc#medicine#health#lifesciences#event#armevents#investor#investorday
19.03.2019 18:40:50
Maybe next time 😂
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Maybe next time 😂...more
19.03.2019 16:10:56
We have six weeks to go in our very first fundraiser for Morris Animal Foundatio
We have six weeks to go in our very first fundraiser for Morris Animal Foundation in honor of Team WAG- Maggie's Legacy. Can you help us reach our goal? Click the link in our bio to understand our reasons behind this. . Also, why are we so passionate about MAF? Because they provide the funding for life-saving scientific research for animals. Read on to learn more about what they are working on with Degenerative Myelopathy at North Carolina State University: . 🔹️What is it- a chronic, progressive and genetic condition that destroys the spinal cord causing a slow deterioration of function in the rear legs, ultimately resulting in paralysis. . 🔹️What's being done- MAF is identifying a gene silencing therapy which will help prevent genetic mutations associated with accumulating SOD1 build up (superoxide dismutase, ironically an antioxidant). This causes nerve cell death leading to paralysis. Interestingly, the gene that plays a role in DM in dogs is the same as ALS in humans. #theyarentjustdogs . 👩‍💻 Learn more at: https://www.morrisanimalfoundation.org/study/ensuring-safety-novel-degenerative-myelopathy-therapy . . . #bulldogmom#onamission#teamwagmaggieslegacy#morrisanimalfoundation#wegotthis#knowledgeispower#holisticpethealth#furbaby#guardian#soulmates#integrativemedicine#functionalmedicine#caninewellness#degenerativemyelopathy#genetherapy
19.03.2019 15:30:43
Informational Drugs represent a new strategy for treating devastating illnesses
Informational Drugs represent a new strategy for treating devastating illnesses at their genetic roots. They take advantage of the cell’s natural mechanisms to prevent defective recipes from being used, or even rewrites the recipes to make them work as many diseases nature intended them to . . . #BluGenesFdn#babies#children#raredisease#taysachsdisease#infant#blugenes#geneticdisorder#infancy#hope#taysachs#showyourrare#rarediseaseawareness#care4rare#awareaboutrare#rarewarrior#genetherapy#research#UMASS#donation#cure#umassmed#linkinprofile#therapy#informationaldrugs#illness#geneticrecipe
19.03.2019 15:30:42
Join Dr Cos and Dr Avi Roy as they discusse#Gene #therapy, #newtech and how it c
Join Dr Cos and Dr Avi Roy as they discusse#Gene#therapy,#newtech and how it can help us live #better,#stronger and #faster. The are a lot of valuable informations to be shared on this podcast. Listen to the whole episode here: https://soundcloud.com/user-480873583/ep-3-picking-your-genes-and-living-how-you-want-to-live-better-stronger-faster-with-avi-roy #genes#genetherapy#medicaladvancements#newtechnology#newtechnologies
19.03.2019 14:42:56
Good luck ladies! #Repost @sfcfoundtn
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🏃‍♀️🏃‍♂️ 👟 BLAZE A TRAIL IN BRISBANE..
Good luck ladies! #Repost@sfcfoundtn ・・・ 🏃‍♀️🏃‍♂️ 👟 BLAZE A TRAIL IN BRISBANE... Getting some decent distances under their belts, these running buddies took to the trails on the weekend. Kirst Milton and Leanne Miller are running alongside their friend Michelle Morrice, mother to Sanfilippo warrior, Alec @hopeforalec in the SF Super Series @brisbanetrailultra to help fund groundbreaking medical research. You can too! REGISTER TO RUN (See link in bio) #medicalresearch#sanfilipposyndrome#hopeforalec#charityrunner#brisbanetrailultra#mumswhorun#runningmotivation#raredisease#hopeforacure#genetherapy#makingadifference#visitbrisbane@brisbanecitycouncil@brisbaneweekender@brisbanecourier@runningmumsaustralia
19.03.2019 08:25:21
#Repost @sfcfoundtn with @get_repost
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🏃‍♀️🏃‍♂️ 👟 BLAZE A TRAIL IN BRISBANE...
#Repost@sfcfoundtn with @get_repost ・・・ 🏃‍♀️🏃‍♂️ 👟 BLAZE A TRAIL IN BRISBANE... Getting some decent distances under their belts, these running buddies took to the trails on the weekend. Kirst Milton and Leanne Miller are running alongside their friend Michelle Morrice, mother to Sanfilippo warrior, Alec @hopeforalec in the SF Super Series @brisbanetrailultra to help fund groundbreaking medical research. You can too! REGISTER TO RUN (See link in bio) #medicalresearch#sanfilipposyndrome#hopeforalec#charityrunner#brisbanetrailultra#mumswhorun#runningmotivation#raredisease#hopeforacure#genetherapy#makingadifference#visitbrisbane@brisbanecitycouncil@brisbaneweekender@brisbanecourier@runningmumsaustralia
19.03.2019 07:58:57
Science Signaling journal cover | Oct 2018
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Online Cover This week features a #
Science Signaling journal cover | Oct 2018 . Online Cover This week features a #ResearchArticle (see also the associated Focus) that describes how the #RNA binding #protein#Arid5a is necessary for #cellular responses to #IL17#cytokine stimulation. The image shows an #illustration of single-strand RNA. [Image: nobeastsofierce/shutterstock.com] #ScienceSignaling#genetics#cellbiology#genetherapy#immunotherapy#biomedicalscience#aaas@sciencemagazine
19.03.2019 07:50:30
🏃‍♀️🏃‍♂️ 👟 BLAZE A TRAIL IN BRISBANE... Getting some decent distances under thei
🏃‍♀️🏃‍♂️ 👟 BLAZE A TRAIL IN BRISBANE... Getting some decent distances under their belts, these running buddies took to the trails on the weekend. Kirst Milton and Leanne Miller are running alongside their friend Michelle Morrice, mother to Sanfilippo warrior, Alec @hopeforalec in the SF Super Series @brisbanetrailultra to help fund groundbreaking medical research. You can too! REGISTER TO RUN (See link in bio) for the Sanfilippo Children’s Foundation in this year’s SF Super Series. #medicalresearch#sanfilipposyndrome#hopeforalec#charityrunner#brisbanetrailultra#mumswhorun#runningmotivation#raredisease#hopeforacure#genetherapy#makingadifference#visitbrisbane@brisbanecitycouncil@brisbaneweekender@brisbanecourier@runningmumsaustralia
19.03.2019 07:45:34
Love this girl! While we’re mainly geared towards pattern and genes that intense
Love this girl! While we’re mainly geared towards pattern and genes that intense or create a change in pattern, this girl packs a punch in that department! She’s a Pinstripe Mojave Black Pastel Trick, pure potential to do some damage in any project and growing fast, she’s just under 700 grams at 10 months old! #snakensteinreptiles#genetherapy#ballpythonsofinstagram#ballpythonmorphs#python#ballpythonbreeder#snakesofinstagram#ballpython#snake
19.03.2019 06:04:20
Getting prepared! Egg incubation tubs, we use the sterilite 7qt with latching li
19.03.2019 05:58:52
Our lovely female Blitz, she’s just starting to build follicles. We had already
Our lovely female Blitz, she’s just starting to build follicles. We had already picked out a male for her this season, might have to revisit that...🤔😉. #snakensteinreptiles#genetherapy#ballpythonsofinstagram#ballpythonmorphs#python#ballpythonbreeder#snakesofinstagram#ballpython#snake
19.03.2019 05:54:19
Another one of our oddball boys, he hasn’t quite fingered out the breeding thing
Another one of our oddball boys, he hasn’t quite fingered out the breeding thing yet this season, but that’s ok! Blitz YB. @granddaddyherps1904#snakensteinreptiles#genetherapy#ballpythonsofinstagram#ballpythonmorphs#python#ballpythonbreeder#snakesofinstagram#ballpython#snake
19.03.2019 05:47:44
Everyone at NF2 Biosolutions is gearing up for a very important day!  On March 2
Everyone at NF2 Biosolutions is gearing up for a very important day! On March 29th, we will welcome professionals in genetics, medicine, research, and more, to work on gene therapy for NF2. #ineedacure#genetherapy#endnf2#neurofibromatosistype2
19.03.2019 05:23:56
Global regenerative medicine market is expected to reach USD 79.8 billion by 202
Global regenerative medicine market is expected to reach USD 79.8 billion by 2024, at a CAGR of 20.5% from 2018 to 2024. #regenerativemedicine#genetherapy#smallmolecules#biologics#biomedicalresearch#celltherapy#regenerativemedicinecenter@novartis@experiencenuva@mimedx@vericelcorp
19.03.2019 04:37:38
Love this! Nothing better than coming home to ovulation #6! Looks like just the
Love this! Nothing better than coming home to ovulation #6! Looks like just the start. 🤞🤞 on this one Ambush x Super Pastel #snakensteinreptiles#genetherapy#ballpythonsofinstagram#ballpythonmorphs#python#ballpythonbreeder#snakesofinstagram#ballpython#snake#ambushproject
19.03.2019 04:17:11
Meet Dr. Weidong Xiong, the ICT U.S research scientist. Originally from China, D
Meet Dr. Weidong Xiong, the ICT U.S research scientist. Originally from China, Dr. Xiong spent time as a clinician and scientist in the UK, and now the U.S. Dr. Xiong is very passionate about exploring the possibility of manipulating genes and cells to be used as therapeutic methods for treating devastating diseases. We’re excited to see what you will discover Dr. Weidong! #meetthestaffmonday#researchscientist#genetherapy#inheritorcelltechnologyus#ictus
19.03.2019 00:58:47
Me...
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Me......more
18.03.2019 21:13:36
Happy St. Patrick’s Day from the little leprechauns, Maxwell and Riley!  Maxwell
Happy St. Patrick’s Day from the little leprechauns, Maxwell and Riley! Maxwell is getting his ☘️ on in the last picture - chugging a bath water car bomb! The twinado turns two in 9 days - so unbelievable. #SLC6A1#milestonesformaxwell#genetherapy
18.03.2019 19:46:37
The next group of girls we’re keeping an eye on! Season is starting to take some
The next group of girls we’re keeping an eye on! Season is starting to take some shape, so far so good! #snakensteinreptiles#genetherapy#ballpythonsofinstagram#ballpythonmorphs#python#ballpythonbreeder#snakesofinstagram#ballpython#snake
18.03.2019 16:09:47
There she blows! Pretty close to peak ovulation! HRA x Pastel, looking great! 🤞🤞
18.03.2019 15:40:59
3 (not so) blind mice: with a single gene insertion, blind mice have regained th
3 (not so) blind mice: with a single gene insertion, blind mice have regained their sight. How fab is it that we may actually have the power to give humans with age-related retinal degeneration their sight back in the near future? 👀 • Very recently, scientists at the University of California inserted a gene for a green-light receptor into the eyes of blind mice. Within a month, they were able to navigate around obstacles as easily as mice with no vision impairments.🐁 • The science bit: researchers designed a virus targeted at retinal ganglion cells and loaded it with a gene for a light-sensitive receptor (opsin). Normally this gene is only expressed by cone photoreceptors cells in the eye, not by ganglion cells. So when injected, the virus carried the gene to the ganglion cells which are usually insensitive to light and made them light-sensitive and able to send signals to the brain interpreted as sight.👩🏻‍🔬 • Within as little as three years, this gene therapy could be tried on humans who’ve suffered retinal degeneration, ideally giving them enough vision to move around, read or watch videos.🧓🏼 . . . #science#neuroscience#mice#3blindmice#notanymore#sciencenews#research#doodle#genetherapy#sight#discovery#berkeley#drawing#interesting#nerd#study#getgrannyhersightback
18.03.2019 13:39:37
This week - Meet us at Bioprocessing Summit Europe 2019! Vironova's Marketing Di
This week - Meet us at Bioprocessing Summit Europe 2019! Vironova's Marketing Director Nina Forsberg will host a Round table, 19th of March at 16:45. Insights are free, but seats limitied, make sure to be there! Our Senior Scientist and Ph. D. Vanessa Carvalho will hold a presentation on March 20th, at 15:15 on the topic - Analysis of Purity and Packaging of Gene Therapy Vectors and VLPs to Support Process Development Decisions. Make sure to attend! Least but not last, check out our MiniTEM™ - A compact and portable TEM, Designed for automated nanoparticle characterization Built by experts for every day users. Bringing software, AI, Big Data and Life Science data into the equation. Makining the invisible visible. Stop by our booth and share your impressions, insights and challenges. __________ #BPSMTeu#lisbon#biotech#vironova#Bioprocessing#makingtheinvisiblevisible#transmissionelectronmicroscopy#genetherapy#MiniTEM#electronmicroscope#transmissionelectonmicroscopemicroscopist#research#biosafety#microbiology#science#medtech#lifescience
18.03.2019 10:13:50
Such an amazing simple two gene combo with so much potential. This guy is alread
Such an amazing simple two gene combo with so much potential. This guy is already over 500 grams and found out he’s producing sperm castings 🤔.... #snakensteinreptiles#genetherapy#ballpythonsofinstagram#ballpythonmorphs#python#ballpythonbreeder#snakesofinstagram#ballpython#snake
18.03.2019 05:41:21
The owner we bought this boy from wants him back 😂. Sorry he’s staying here! Rea
The owner we bought this boy from wants him back 😂. Sorry he’s staying here! Really starting to get his colors in. Second best from hatching is buying as hatchlings. #snakensteinreptiles#genetherapy#ballpythonsofinstagram#ballpythonmorphs#python#ballpythonbreeder#snakesofinstagram#ballpython#snake
18.03.2019 05:39:22
Every time we want to get a picture of this guy he’s in shed. Well after a fresh
Every time we want to get a picture of this guy he’s in shed. Well after a fresh shed, Ultramel Het Ghost looking slick. #snakensteinreptiles#genetherapy#ballpythonsofinstagram#ballpythonmorphs#python#ballpythonbreeder#snakesofinstagram#ballpython#snake
18.03.2019 05:35:32
This science-y #cartoon depicts a #virus grabbing a “receptor.” Receptors are pr
This science-y #cartoon depicts a #virus grabbing a “receptor.” Receptors are proteins found on cell surfaces. Receptors have a bunch of important functions, but viruses use them as handles. With a good hold on a receptor, a virus can effectively infect a cell. Learn more about receptors and how they’re used in #GeneTherapy on my blog. #Biology#Virology#SciArt#Drawing#SciComm#GeneticEngineering.
18.03.2019 03:36:58
I accepted the #SMASHSMARD challenge to help raise funds and awareness for my ba
I accepted the #SMASHSMARD challenge to help raise funds and awareness for my baby cousin, Nash! 💪🏻 💙 @smashsmard My cousins, Brittany Stineman and Bobby Stineman, have created a nonprofit organization, smash SMARD, to help raise both funds and awareness for this disease. I now nominate @hankoliverpug and my family and friends to help to complete the challenge and donate! Ready....set....#SMASHSMARD !! DONATE TODAY: www.smashSMARD.org/donate 🔬Gene Therapy IS the solution, but it’s VERY expensive. $3 million expensive! EVERY PENNY COUNTS & Will fund SMARD1 #GeneTherapy research at Nationwide Children’s Hospital
17.03.2019 22:56:41
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